RareCare Patient Assistance Programs is a suite of programs from the National Organization for Rare Disorders (NORD) that funds financial assistance for individuals living with rare diseases.

Since 1987, NORD has offered programs covering life-saving medications, insurance premium and co-pay assistance, diagnostic testing, travel assistance for clinical trials or specialist consultations, caregiver respite, emergency relief, and educational support. Programs vary by rare disease and may be open for applications, waitlisting, or closed depending on current funding.

Eligible applicants are individuals diagnosed with qualifying rare diseases who cannot otherwise afford critical treatments or care.

Patient Assistance Programs - National Organization for Rare Disorders Patient & Caregiver Assistance Rare Disease Centers of Excellence Sobre los Centros de Excelencia Apply (Medical Institutions only) Information on Clinical Trials & Research Studies Find Clinical Trials & Research Studies Finding a Support Organization RareEdu ® – Online Learning Platform NORD provides more including our Rare Disease Educational Support Program and Rare Caregiver Respite Program .

Patient Assistance Programs NORD’s Patient Assistance Programs Since 1987, NORD has provided assistance programs to help patients obtain life-saving or life-sustaining medication they could not otherwise afford. These programs provide medication, financial assistance with insurance premiums and co-pays, diagnostic testing assistance, and travel assistance for clinical trials or consultation with disease specialists.

Filter by Program Status > Select an option Accepting Applications Accepting new applications and re-enrollments for current year Accepting new applications and re-enrollments for next year Closed Not yet accepting applications for current year Referral Required Temporarily Waitlisting Filter by Program Types > Select an option Clinical Trial Support Emergency Relief Program Medical Assistance Premium and Copay Accepting Applications --> Acid Sphingomyelinase Deficiency (ASMD) Medical Assistance ASMD PremiumCopay&MedicalAssistanceAug2024 Accepting Applications --> Acid Sphingomyelinase Deficiency (ASMD) Premium Copay ASMD PremiumCopay&MedicalAssistanceAug2024 Accepting new applications and re-enrollments for current year --> Alpha-1 Antitrypsin Deficiency Premium Copay Assistance Accepting new applications and re-enrollments for current year Alpha-1 PremiumCopayAssistance-July2024 Temporarily Waitlisting --> Amyloidosis Medical Assistance Temporarily Waitlisting --> Amyloidosis Premium Copay Assistance Accepting Applications --> Amyotrophic Lateral Sclerosis (ALS) Travel & Lodging Assistance AT-01 Phase 3 Imaging Study AT01-301 Phase 3 Imaging Agent Study_flyer 12_04_24 Accepting Applications --> atypical Hemolytic Uremic Syndrome (aHUS) Emergency Relief Accepting new applications and re-enrollments for current year --> atypical Hemolytic Uremic Syndrome (aHUS) Medical Assistance Accepting new applications and re-enrollments for current year aHUS_PremiumCopay&MedicalAssistance-July2024 Accepting new applications and re-enrollments for current year --> atypical Hemolytic Uremic Syndrome (aHUS) Premium Copay Assistance Accepting new applications and re-enrollments for current year aHUS_PremiumCopay&MedicalAssistance-July2024 Accepting Applications --> Autoimmune Pulmonary Alveolar Proteinosis (aPAP) Medical Assistance aPAP T&L Assistance2026 (1) Azitra NTH-1201 Study Travel Assistance NTH-1201 (NethertonSyndrome) -Azitra-June2024 Accepting new applications and re-enrollments for current year --> Bardet-Biedl Syndrome (BBS) Premium Copay Assistance Accepting new applications and re-enrollments for current year PAP_PremCopay_BBS flyer , PAP_PremCopay_BBS-flyer SPANISH Accepting Applications --> Barth Syndrome Emergency Relief BarthSyndrome ERF Revised -3-2023 Accepting Applications --> Barth Syndrome Travel Assistance Fund 2026 Barth Syndrome Foundation Family Services Fund (3) Batten Disease Emergency Relief Accepting Applications --> Batten Disease Medical Assistance Batten-PremiumCopayMedicalAssist-2026 (2) Accepting new applications and re-enrollments for current year --> Batten Disease Premium Copay Assistance Accepting new applications and re-enrollments for current year Batten-PremiumCopayMedicalAssist-2026 (2) Accepting new applications and re-enrollments for current year --> Bile Acid Synthesis and Zellweger Spectrum Disorders Medical Assist Accepting new applications and re-enrollments for current year BASD_ZSD-PremiumCopay&MedicalAssistance Accepting new applications and re-enrollments for current year --> Bile Acid Synthesis and Zellweger Spectrum Disorders Premium Copay Assistance Accepting new applications and re-enrollments for current year BASD_ZSD-PremiumCopay&MedicalAssistance Accepting new applications and re-enrollments for current year --> Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN) Copay Assistance Accepting new applications and re-enrollments for current year Accepting Applications --> Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN) Emergency Relief Accepting Applications --> Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN) Travel & Lodging Assistance Accepting Applications --> Cerebrotendinous Xanthomatosis (CTX) Medical Assistance CTX-PremCopay&Medical Assist-2026 Accepting new applications and re-enrollments for current year --> Cerebrotendinous Xanthomatosis (CTX) Premium Copay Assistance Accepting new applications and re-enrollments for current year CTX-PremCopay&Medical Assist-2026 Chronic Granulomatous Disease (CGD) Copay Assistance CGD-PAP , CGD-PAP-Spanish Chronic Granulomatous Disease (CGD) Medical Assistance CGD-PAP , CGD-PAP-Spanish Accepting new applications and re-enrollments for current year --> Chronic inflammatory demyelinating polyneuropathy (CIDP) Medical Assistance Accepting new applications and re-enrollments for current year CIDP-PremiumCopay&MedicalAssistance-Jan.

2025 (4) Accepting new applications and re-enrollments for current year --> Chronic inflammatory demyelinating polyneuropathy (CIDP) Premium Copay Assistance Accepting new applications and re-enrollments for current year CIDP-PremiumCopay&MedicalAssistance-Jan.

2025 (4) Accepting new applications and re-enrollments for current year --> Classical Homocystinuria (HCU) Medical Assistance Accepting new applications and re-enrollments for current year MedicalAssist_Classical HCU-2026 (6) CureDuchenne Educational T&L Support CureDuchenne Educational Support T&L , CureDuchenne Educational Support T&L- Spanish Accepting new applications and re-enrollments for current year --> Cushings Syndrome Medical Assistance Accepting new applications and re-enrollments for current year Cushing's-PremCopay&Medical Assist-Aug2024 Accepting new applications and re-enrollments for current year --> Cushings Syndrome Premium Copay Assistance Accepting new applications and re-enrollments for current year Cushing's-PremCopay&Medical Assist-Aug2024 Accepting new applications and re-enrollments for current year --> Cystinosis Copay Assistance Accepting new applications and re-enrollments for current year Cystinosis-Copay&MedicalAssistance-Aug2024 Accepting new applications and re-enrollments for current year --> Cystinosis Medical Assistance Accepting new applications and re-enrollments for current year Cystinosis-Copay&MedicalAssistance-Aug2024 Accepting new applications and re-enrollments for current year --> Cystinuria Medical Assistance Accepting new applications and re-enrollments for current year Cystinuria-PremCopay&Medical Assist-Aug2024 Accepting new applications and re-enrollments for current year --> Cystinuria Premium Copay Assistance Accepting new applications and re-enrollments for current year Cystinuria-PremCopay&Medical Assist-Aug2024 DISC-1459 Erythropoietic Protoporphyria (EPP) Study Travel & Lodging Assistance Accepting new applications and re-enrollments for current year --> Duchenne Muscular Dystrophy Medical Assistance Accepting new applications and re-enrollments for current year DMD-PremiumCopay&MedicalAssistanceAugust2024 , DMD-PremiumCopay&MedicalAssistance-Spanish (1) Accepting new applications and re-enrollments for current year --> Duchenne Muscular Dystrophy Premium Copay Assistance Accepting new applications and re-enrollments for current year DMD-PremiumCopay&MedicalAssistanceAugust2024 , DMD-PremiumCopay&MedicalAssistance-Spanish (1) Accepting Applications --> Eva’s Butterfly Wishes Experience for Rare Children (5 and under) Eva's Butterfly Wishes-2025 Accepting Applications --> Fabry Disease Medical Assistance Fabry_PremiumCopay&MedicalAssistanceJuly2024 Accepting Applications --> Fabry Disease Premium Copay Assistance Fabry_PremiumCopay&MedicalAssistanceJuly2024 Not yet accepting applications for current year --> Floxuridine Medication Assistance Not yet accepting applications for current year Floxuridine-Medication Assistance 2025 (1) Accepting new applications and re-enrollments for current year --> Gaucher Disease Medical Assistance Accepting new applications and re-enrollments for current year Gaucher-PremCopay&Medical Assist-March2025 Accepting new applications and re-enrollments for current year --> Gaucher Disease Premium Copay Assistance Accepting new applications and re-enrollments for current year Gaucher-PremCopay&Medical Assist-March2025 Accepting Applications --> Guillain-Barre Emergency Relief Assistance PAP_EmergRelief_GBS-July2024 Accepting new applications and re-enrollments for current year --> Hunter Syndrome Medical Assistance Accepting new applications and re-enrollments for current year HunterSyndrome-PremiumCopay&MedicalAssistanceAug2024 (1) Accepting new applications and re-enrollments for current year --> Hunter Syndrome Premium Copay Assistance Accepting new applications and re-enrollments for current year HunterSyndrome-PremiumCopay&MedicalAssistanceAug2024 (1) Accepting Applications --> Hypophosphatasia (HPP) Emergency Relief For Patients & Caregivers For Clinicians & Researchers Make 2026 Count: Gift research, care, and advocacy for families everywhere Your gift today fuels progress in the lab, in clinics, on Capitol Hill and for rare families who can’t wait another year for answers.

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